41
TITLE: PHASE 2 OPEN-LABEL EXTENSION STUDY OF PATISIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC FOR THE TREATMENT OF FAMILIAL AMYLOID POLYNEUROPATHY
AUTHORS: David Adams; Ole Suhr; Isabel Conceicao; Marcia Waddington Cruz; Hartmut Schmidt; Juan Buades; Josep Campistol; Jean Pouget; John Berk; Teresa Coelho;
PUBLISHED: 2015, SOURCE: Annual Meeting of the Association-of-British-Neurologists (ABN) in JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, VOLUME: 86, ISSUE: 11
INDEXED IN: WOS CrossRef
42
TITLE: Guideline of transthyretin-related hereditary amyloidosis for clinicians  Full Text
AUTHORS: Yukio Ando; Teresa Coelho; John L Berk; Marcia Waddington Cruz; Bo Goran Ericzon; Shu ichi Ikeda; David D Lewis; Laura Obici; Violaine Plante Bordeneuve; Claudio Rapezzi; Gerard Said; Fabrizio Salvi;
PUBLISHED: 2013, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 8, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
Page 5 of 5. Total results: 42.