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TITLE: mRNA Degradation as a Therapeutic Solution for Mucopolysaccharidosis Type IIIC: Use of Antisense Oligonucleotides to Promote Downregulation of Heparan Sulfate Synthesis  Full Text
AUTHORS: Santos, Juliana Ines; Goncalves, Mariana; Almeida, Matilde Barbosa; Rocha, Hugo; Duarte, Ana Joana; Matos, Liliana; Moreira, Luciana Vaz; Encarnacao, Marisa; Gaspar, Paulo; Prata, Maria Joao; Coutinho, Maria Francisca; Alves, Sandra;
PUBLISHED: 2025, SOURCE: INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES, VOLUME: 26, ISSUE: 3
INDEXED IN: Scopus WOS CrossRef
IN MY: ORCID
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TITLE: António Amorim (in memoriam)
AUTHORS: Maria João Prata; Leonor Gusmão; Iva Gomes; Nádia Pinto; Sandra Martins; Verónica Gomes; Angel Carracedo;
PUBLISHED: 2025, SOURCE: Forensic Science International: Genetics
INDEXED IN: Scopus