1
TITLE: Allele-Specific Silencing of Mutant ATXN3 Mitigates Motor Deficits and Neuropathology in a Severely Impaired Mouse Model of Spinocerebellar Ataxia Type 3 (SCA3)
AUTHORS: Silva, Ana Carolina; Henriques, Carina; Lobo, Diana; Fernandes, Ana Rita; Lopes, Miguel; Pereira, Dina; Duarte, Sonia; Baganha, Rafael; Lopes, Sara; Santana, Magda; Nobre, Rui Jorge; de Almeida, Luis Pereira;
PUBLISHED: 2024, SOURCE: MOLECULAR THERAPY, VOLUME: 32, ISSUE: 4
INDEXED IN: WOS
2
TITLE: Isolation of Natural and Biologically Active EV-AAVs for Brain Gene Delivery
AUTHORS: Henriques, Carina; Lopes, Miguel; Albuquerque, Patricia; Rufino Ramos, David; Gaspar, Laetitia; Lobo, Diana; Silva, Ana Carolina; Baganha, Rafael; Duarte, Sonia; Maguire, Casey A.; Santana, Magda; de Almeida, Luis Pereira; Nobre, Rui Jorge;
PUBLISHED: 2023, SOURCE: MOLECULAR THERAPY, VOLUME: 31, ISSUE: 4
INDEXED IN: WOS
3
TITLE: Isolation of Biologically Active Extracellular Vesicles-Associated AAVs for Gene Delivery to the Brain by Size Exclusion Chromatography
AUTHORS: Carina Henriques; Miguel M Lopes; Patrícia Albuquerque; David Rufino-Ramos; Laetitia S Gaspar; Diana Lobo; Kevin Leandro; Ana Carolina Silva; Rafael Baganha; Sónia Duarte; Casey A Maguire; Magda Santana; Luís Pereira de Almeida; Rui Jorge Nobre;
PUBLISHED: 2023
INDEXED IN: CrossRef