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TITLE: Rapid progression of familial amyloidotic polyneuropathy A multinational natural history study
AUTHORS: David Adams; Teresa Coelho; Laura Obici; Giampaolo Merlini; Zoia Mincheva; Narupat Suanprasert; Brian R Bettencourt; Jared A Gollob; Pritesh J Gandhi; William J Litchy; Peter J Dyck;
PUBLISHED: 2015, SOURCE: NEUROLOGY, VOLUME: 85, ISSUE: 8
INDEXED IN: Scopus WOS CrossRef
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TITLE: Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study  Full Text
AUTHORS: Ole B Suhr; Teresa Coelho; Juan Buades; Jean Pouget; Isabel Conceicao; John Berk; Hartmut Schmidt; Marcia Waddington Cruz; Josep M Campistol; Brian R Bettencourt; Akshay Vaishnaw; Jared Gollob; David Adams;
PUBLISHED: 2015, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 10, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
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TITLE: Safety and Efficacy of RNAi Therapy for Transthyretin Amyloidosis
AUTHORS: Teresa Coelho; David Adams; Ana Silva; Pierre Lozeron; Philip N Hawkins; Timothy Mant; Javier Perez; Joseph Chiesa; Steve Warrington; Elizabeth Tranter; Malathy Munisamy; Rick Falzone; Jamie Harrop; Jeffrey Cehelsky; Brian R Bettencourt; Mary Geissler; James S Butler; Alfica Sehgal; Rachel E Meyers; Qingmin M Chen; Todd Borland; Renta M Hutabarat; Valerie A Clausen; Rene Alvarez; Kevin Fitzgerald; Christina Gamba Vitalo; Saraswathy V Nochur; Akshay K Vaishnaw; Dinah W Y Sah; Jared A Gollob; Ole B Suhr; ...More
PUBLISHED: 2013, SOURCE: NEW ENGLAND JOURNAL OF MEDICINE, VOLUME: 369, ISSUE: 9
INDEXED IN: Scopus WOS CrossRef