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TITLE: Multi-domain impact of elosufase alfa in Morquio A syndrome in the pivotal phase III trial  Full Text
AUTHORS: Hendriksz, CJ; Giugliani, R; Harmatz, P; Mengel, E; Guffon, N; Valayannopoulos, V; Parini, R; Hughes, D; Pastores, GM; Lau, HA; Al Sayed, MD; Raiman, J; Ben Omran, T; Bober, MB; Burton, BK; Cleary, MA; Dali, CI; de Medeiros, PFV; Guelbert, NB; Hiwot, TG; Jin, DK; Jones, SA; Lin, SP; Maranda, B; Mitchell, JJ; Murphy, EM; Muschol, N; Okuyama, T; Santra, S; Villarreal, MLS; Steiner, R; Tanpaiboon, P; Valente, PC; Matos, SBG; Vellodi, A; White, KK; Wijburg, FA; Yang, K; Mealiffe, M; Haller, C; ...More
PUBLISHED: 2015, SOURCE: Molecular Genetics and Metabolism, VOLUME: 114, ISSUE: 2
INDEXED IN: Scopus CrossRef