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TITLE: Nonclinical data supporting orphan medicinal product designations in the area of rare infectious diseases  Full Text
AUTHORS: Maria E Sheean; Eva Malikova; Dinah Duarte; Giuseppe Capovilla; Laura Fregonese; Matthias P Hofer; Armando Magrelli; Segundo Mariz; Fernando Mendez Hermida; Robert Nistico; Tim Leest; Nikolaos V Sipsas; Stelios Tsigkos; Dinko Vitezic; Kristina Larsson; Bruno Sepodes; Violeta Stoyanova Beninska;
PUBLISHED: 2020, SOURCE: DRUG DISCOVERY TODAY, VOLUME: 25, ISSUE: 2
INDEXED IN: Scopus WOS
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TITLE: Defining orphan conditions in the context of the European orphan regulation: challenges and evolution
AUTHORS: Daniel J O'Connor; Maria E Sheean; Matthias P Hofer; Stelios Tsigkos; Segundo Mariz; Laura Fregonese; Kristina Larsson; Virginie Hivert; Kerstin Westermark; Frauke Naumann Winter; Violeta Stoyanova Beninska; Ingeborg Barisic; Giuseppe Capovilla; Armando Magrelli; Bruno Sepodes;
PUBLISHED: 2019, SOURCE: NATURE REVIEWS DRUG DISCOVERY, VOLUME: 18, ISSUE: 7
INDEXED IN: WOS
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TITLE: Establishing rarity in the context of orphan medicinal product designation in the European Union  Full Text
AUTHORS: Stelios Tsigkos; Matthias Philipp Hofer; Maria Elzbieta Sheean; Segundo Mariz; Kristina Larsson; Frauke Naumann Winter; Laura Fregonese; Bruno Sepodes;
PUBLISHED: 2018, SOURCE: DRUG DISCOVERY TODAY, VOLUME: 23, ISSUE: 3
INDEXED IN: WOS