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TITLE: Oral treatment for mucopolysaccharidosis VI: Outcomes of the first phase IIa study with odiparcil  Full Text
AUTHORS: Guffon, Nathalie; Chowdary, Pratima; Teles, Elisa Leao; Hughes, Derralynn; Hennermann, Julia B.; Huot Marchand, Philippe; Faudot Vernier, Elodie; Lacombe, Olivier; Fiquet, Anne; Richard, Marie Paule; Abitbol, Jean Louis; Tallandier, Mireille; Hendriksz, Christian J.;
PUBLISHED: 2022, SOURCE: JOURNAL OF INHERITED METABOLIC DISEASE, VOLUME: 45, ISSUE: 2
INDEXED IN: Scopus WOS