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TITLE: Finding new drugs to enhance anion secretion in cystic fibrosis: Toward suitable systems for better drug screening. Report on the pre-conference meeting to the 12th ECFS Basic Science Conference, Albufeira, 25-28 March 2015  Full Text
AUTHORS: Alan S Verkman; Aleksander Edelman; Margarida Amaral; Marcus A Mall; Jeffrey M Beekman; Torsten Meiners; Luis J V Galietta; Christine E Bear;
PUBLISHED: 2015, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 14, ISSUE: 6
INDEXED IN: Scopus WOS CrossRef
IN MY: ORCID
72
TITLE: Hallmarks of therapeutic management of the cystic fibrosis functional landscape  Full Text
AUTHORS: Margarida D Amaral; William E Balch;
PUBLISHED: 2015, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 14, ISSUE: 6
INDEXED IN: Scopus WOS CrossRef
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73
TITLE: Increased efficacy of VX-809 in different cellular systems results from an early stabilization effect of F508del-CFTR
AUTHORS: Farinha, CM; Sousa, M; Canato, S; Schmidt, A; Uliyakina, I; Amaral, MD;
PUBLISHED: 2015, SOURCE: PHARMACOLOGY RESEARCH & PERSPECTIVES, VOLUME: 3, ISSUE: 4
INDEXED IN: Scopus WOS CrossRef
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74
TITLE: Abnormal Protein Glycosylation and Activated PI3K/Akt/mTOR Pathway: Role in Bladder Cancer Prognosis and Targeted Therapeutics  Full Text
AUTHORS: Ceu Costa; Sofia Pereira; Luis Lima ; Andreia Peixoto; Elisabete Fernandes; Diogo Neves; Manuel Neves; Cristiana Gaiteiro; Ana Tavares; Rui M G Gil da Costa ; Ricardo Cruz; Teresina Amaro; Paula A Oliveira; Jose Alexandre Ferreira; Lucio L Santos;
PUBLISHED: 2015, SOURCE: PLOS ONE, VOLUME: 10, ISSUE: 11
INDEXED IN: Scopus WOS CrossRef: 56
75
TITLE: HOW TO TARGET DIFFERENT COMBINATIONS OF CFTR MUTATIONS  Full Text
AUTHORS: Margarida S Amaral;
PUBLISHED: 2015, SOURCE: PEDIATRIC PULMONOLOGY, VOLUME: 50
INDEXED IN: WOS
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TITLE: CFTR functional measurements in human models for diagnosis, prognosis and personalized therapy: Report on the pre-conference meeting to the 11th ECFS Basic Science Conference, Malta, 26-29 March 2014  Full Text
AUTHORS: Jeffrey M Beekman; Isabelle Sermet Gaudelus; Kris de Boeck; Tanja Gonska; Nico Derichs; Marcus A Mall; Anil Mehta; Ulrich Martin; Mitch Drumm; Margarida D Amaral;
PUBLISHED: 2014, SOURCE: JOURNAL OF CYSTIC FIBROSIS, VOLUME: 13, ISSUE: 4
INDEXED IN: Scopus WOS
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TITLE: Experimental Assessment of Splicing Variants Using Expression Minigenes and Comparison with In Silico Predictions  Full Text
AUTHORS: Neeraj Sharma; Patrick R Sosnay; Anabela S Ramalho; Christopher Douville; Arianna Franca; Laura B Gottschalk; Jeenah Park; Melissa Lee; Briana Vecchio Pagan; Karen S Raraigh; Margarida D Amara; Rachel Karchin; Garry R Cutting;
PUBLISHED: 2014, SOURCE: HUMAN MUTATION, VOLUME: 35, ISSUE: 10
INDEXED IN: Scopus WOS CrossRef
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TITLE: Quantitative Evaluation of DNA Dissociation from Liposome Carriers and DNA Escape from Endosomes During Lipid-Mediated Gene Delivery
AUTHORS: Salome Magalhaes; Sofia Duarte; Gabriel A Monteiro; Fabio Fernandes;
PUBLISHED: 2014, SOURCE: HUMAN GENE THERAPY METHODS, VOLUME: 25, ISSUE: 5
INDEXED IN: Scopus WOS
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