31
TÍTULO: Open-label extension of NEURO-TTR study in patients with hereditary transthyretin (hATTR) amyloidosis: Long-term update  Full Text
AUTORES: Thomas Brannagan; Annabel Wang; Teresa Coelho; Marcia Waddington Cruz; Michael Polydefkis; Peter Dyck; Violaine Plante Bordeneuve; John Berk; Fabio Barroso; David Adams; Giampaolo Merlini; Isabel Conceicao; Brett Monia; Steven Hughes; Jesse Kwoh; Shiangtung Jung; Brenda Baker; Elizabeth Ackermann; Merrill Benson; Morie Gertz;
PUBLICAÇÃO: 2018, FONTE: Annual Meeting of the Peripheral-Nerve-Society in JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 23, NÚMERO: 4
INDEXADO EM: WOS
32
TÍTULO: Safety and efficacy of inotersen in patients with hereditary transthyretin amyloidosis with polyneuropathy (NEURO-TTR)  Full Text
AUTORES: Morie Gertz; Annabel Wang; Teresa Coelho; Marcia Waddington Cruz; Michael Polydefkis; Peter Dyck; Morton Scheinberg; Violaine Plante Bordeneuve; John Berk; Fabio Barroso; Thomas Brannagan; Sami Khella; Isabel Conceicao; Peter Gorevic; Brett Monia; Merrill Benson;
PUBLICAÇÃO: 2018, FONTE: Annual Meeting of the Peripheral-Nerve-Society in JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 23, NÚMERO: 4
INDEXADO EM: WOS
33
TÍTULO: Burden of Hereditary Transthyretin Amyloidosis With Polyneuropathy in Patients Enrolled in the Phase 3 Study NEURO-TTR
AUTORES: John Berk; Annabel K Wang; Teresa Coelho; Marcia Waddington Cruz; Michael J Polydefkis; Peter J Dyck; Morton Scheinberg; Violaine Plante Bordeneuve; Fabio Barroso; David Adams; Thomas Brannagan; Carol Whelan; Brian M Drachman; Stephen B Heitner; Isabel Conceicao; Hartmut Schmidt; Giuseppe Vita; Josep M Campistol; Josep Gamez; Edward Gane; Peter Gorevic; Acary Souza B Bulle Oliveira; Brett P Monia; Stephen G Hughes; Jesse Kwoh; Bradley W McEvoy; Brenda F Baker; Elizabeth J Ackermann; Spencer Guthrie; Asia Sikora Kessler; Morie Gertz; Merrill D Benson; Giampaolo Merlini; ...Mais
PUBLICAÇÃO: 2018, FONTE: 70th Annual Meeting of the American-Academy-of-Neurology (AAN) in NEUROLOGY, VOLUME: 90
INDEXADO EM: WOS
34
TÍTULO: Open Label Extension of the Phase 3 Study NEURO-TTR to Assess the Long-term Efficacy and Safety of Inotersen in Patients With Hereditary Transthyretin Amyloidosis
AUTORES: Thomas Brannagan; Annabel K Wang; Teresa Coelho; Marcia Waddington Cruz; Michael J Polydefkis; Peter J Dyck; Morton Scheinberg; Violaine Plante Bordeneuve; John Berk; Fabio Barroso; David Adams; Carol Whelan; Giampaolo Merlini; Brian M Drachman; Stephen B Heitner; Isabel Conceicao; Hartmut Schmidt; Giuseppe Vita; Josep M Campistol; Josep Gamez; Peter Gorevic; Brett P Monia; Steven G Hughes; Jesse Kwoh; Bradley W McEvoy; Brenda F Baker; Elizabeth J Ackermann; Merrill D Benson; Morie Gertz; ...Mais
PUBLICAÇÃO: 2018, FONTE: 70th Annual Meeting of the American-Academy-of-Neurology (AAN) in NEUROLOGY, VOLUME: 90
INDEXADO EM: WOS
35
TÍTULO: Safety and Efficacy of Inotersen in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy (NEURO-TTR)
AUTORES: Morie Gertz; Annabel K Wang; Teresa Coelho; Marcia Waddington Cruz; Michael J Polydefkis; Peter J Dyck; Morton Scheinberg; Violaine Plante Bordeneuve; John Berk; Fabio Barroso; David Adams; Thomas Brannagan; Carol Whelan; Giampaolo Merlini; Brian M Drachman; Stephen B Heitner; Isabel Conceicao; Harmut Schmidt; Giuseppe Vita; Josep M Campistol; Josep Gamez; Edward Gane; Peter Gorevic; Acary Souza Bulle Oliveira; Brett P Monia; Steven G Hughes; Jesse Kwoh; Bradley W McEvoy; Brenda F Baker; Elizabeth J Ackermann; Merrill D Benson; ...Mais
PUBLICAÇÃO: 2018, FONTE: 70th Annual Meeting of the American-Academy-of-Neurology (AAN) in NEUROLOGY, VOLUME: 90
INDEXADO EM: WOS
36
TÍTULO: Inotersen Improves Norfolk Quality of Life-Diabetic Neuropathy Measures in Patients With Hereditary Transthyretin Amyloidosis with Polyneuropathy in the Phase 3 Study NEURO-TTR
AUTORES: Michael J Polydefkis; Teresa Coelho; Marcia Waddington Cruz; Peter J Dyck; Morton Scheinberg; Violaine Plante Bordeneuve; John Berk; Fabio Barroso; David Adams; Thomas Brannagan; Carol Whelan; Giampaolo Merlini; Brian M Drachman; Stephen B Heitner; Isabel Conceicao; Hartmut Schmidt; Giuseppe Vita; Josep M Campistol; Josep Gamez; Edward Gane; Peter Gorevic; Acary Souza B Bulle Oliveira; Brett P Monia; Steven G Hughes; Jesse Kwoh; Bradley W McEvoy; Brenda F Baker; Elizabeth J Ackermann; Morie Gertz; Merrill D Benson; Annabel K Wang; ...Mais
PUBLICAÇÃO: 2018, FONTE: 70th Annual Meeting of the American-Academy-of-Neurology (AAN) in NEUROLOGY, VOLUME: 90
INDEXADO EM: WOS
37
TÍTULO: Peptide probes detect misfolded transthyretin oligomers in plasma of hereditary amyloidosis patients
AUTORES: Joseph D Schonhoft; Cecilia Monteiro; Lars Plate; Yvonne S Eisele; John M Kelly; Daniel Boland; Christopher G Parker; Benjamin F Cravatt; Sergio Teruya; Stephen Helmke; Mathew Maurer; John Berk; Yoshiki Sekijima; Marta Novais; Teresa Coelho; Evan T Powers; Jeffery W Kelly;
PUBLICAÇÃO: 2017, FONTE: SCIENCE TRANSLATIONAL MEDICINE, VOLUME: 9, NÚMERO: 407
INDEXADO EM: Scopus WOS
38
TÍTULO: Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study  Full Text
AUTORES: Ole B Suhr; Teresa Coelho; Juan Buades; Jean Pouget; Isabel Conceicao; John Berk; Hartmut Schmidt; Marcia Waddington Cruz; Josep M Campistol; Brian R Bettencourt; Akshay Vaishnaw; Jared Gollob; David Adams;
PUBLICAÇÃO: 2015, FONTE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 10, NÚMERO: 1
INDEXADO EM: Scopus WOS CrossRef
39
TÍTULO: Diagnosis, Prognosis, and Therapy of Transthyretin Amyloidosis  Full Text
AUTORES: Morie A Gertz; Merrill D Benson; Peter J Dyck; Martha Grogan; Terresa Coelho; Marcia Cruz; John L Berk; Violaine Plante Bordeneuve; Hartmut H J Schmidt; Giampaolo Merlini;
PUBLICAÇÃO: 2015, FONTE: JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, VOLUME: 66, NÚMERO: 21
INDEXADO EM: WOS CrossRef
40
TÍTULO: PHASE 2 OPEN-LABEL EXTENSION STUDY OF PATISIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC FOR THE TREATMENT OF FAMILIAL AMYLOID POLYNEUROPATHY
AUTORES: David Adams; Ole Suhr; Isabel Conceicao; Marcia Waddington Cruz; Hartmut Schmidt; Juan Buades; Josep Campistol; Jean Pouget; John Berk; Teresa Coelho;
PUBLICAÇÃO: 2015, FONTE: Annual Meeting of the Association-of-British-Neurologists (ABN) in JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, VOLUME: 86, NÚMERO: 11
INDEXADO EM: WOS CrossRef
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