A Brazilian Patient with Late Infantile Metachromatic Leukodystrophy Treated with Lentiviral Hematopoietic Stem-Cell Gene Therapy: A Report from Prenatal Diagnosis to Early Treatment

AuthID
P-00Y-Z1H
21
Author(s)
Iop, G
·
da Silva, LAL
·
Borges, HBL
·
Netto, ABO
·
Brusius-Facchin, AC
·
Leistner-Segal, S
·
Gus, R
·
Sanseverino, MTV
·
[+1]·
Pasetto, FB
·
Sebastiao, FM
·
Silva, TO
·
Magalhaes, JAA
·
de Souza, CFM
·
Recupero, S
·
Calbi, V
·
Fumagalli, F
·
Aiuti, A
·
Giugliani, R
Document Type
Abstract
Year published
2023
Published
in MOLECULAR GENETICS AND METABOLISM, ISSN: 1096-7192
Volume: 138, Issue: 2, Pages: 40-41 (2)
Conference
19Th Annual World Symposium, Date: FEB 21-26, 2023, Location: FL
Indexing
Publication Identifiers
Wos: WOS:001013039500112
Source Identifiers
ISSN: 1096-7192
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Name Order Nome   Name Order Nome   Name Order Nome
1 Faqueti, L;   2 Iop, G;   3 da Silva, LAL;
4 Kubaski, F;   5 Borges, HBL;   6 Netto, ABO;
7 Brusius-Facchin, AC;   8 Leistner-Segal, S;   9 Gus, R;
10 Sanseverino, MTV;   11 Michelin-Tirelli, K;   12 Pasetto, FB;
13 Sebastiao, FM;   14 Silva, TO;   15 Magalhaes, JAA;
16 de Souza, CFM;   17 Recupero, S;   18 Calbi, V;
19 Fumagalli, F;   20 Aiuti, A;   21 Giugliani, R;