1
TITLE: Patient-reported, observer-reported and performance outcomes in qualification procedures at the European Medicines Agency 2013-2018  Full Text
AUTHORS: Silva, Marcio; Moseley, Jane; Vetter, Thorsten; Regnstrom, Jan; Tome, Maria; Aarum, Stiina; Cerreta, Francesca; Schabel, Elmer; Vamvakas, Spiros;
PUBLISHED: 2023, SOURCE: BRITISH JOURNAL OF CLINICAL PHARMACOLOGY
INDEXED IN: Scopus WOS
2
TITLE: Erratum to: Establishing medical plausibility in the context of orphan medicines designation in the European Union  Full Text
AUTHORS: Stelios Tsigkos; Segundo Mariz; Jordi Llinares; Laura Fregonese; Stiina Aarum; Frauke Naumann-Winter; Kerstin Westermark; Bruno Sepodes;
PUBLISHED: 2015, SOURCE: Orphanet Journal of Rare Diseases - Orphanet J Rare Dis, VOLUME: 10, ISSUE: 1
INDEXED IN: CrossRef
3
TITLE: Establishing medical plausibility in the context of orphan medicines designation in the European Union (vol 9, 175, 2014)  Full Text
AUTHORS: Stelios Tsigkos; Segundo Mariz; Jordi Llinares; Laura Fregonese; Stiina Aarum; Frauke Naumann Winter; Kerstin Westermark; Bruno Sepodes;
PUBLISHED: 2015, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 10
INDEXED IN: WOS
4
TITLE: Use of biomarkers in the context of orphan medicines designation in the European Union  Full Text
AUTHORS: Stelios Tsigkos; Jordi Llinares; Segundo Mariz; Stiina Aarum; Laura Fregonese; Bozenna Dembowska Baginska; Rembert Elbers; Pauline Evers; Tatiana Foltanova; Andre Lhoir; Ana Correa Nunes; Daniel O'Connor; Albertha Voordouw; Kerstin Westermark; Bruno Sepodes;
PUBLISHED: 2014, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 9, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
5
TITLE: The orphan framework as a new opportunity: an expert opinion
AUTHORS: Segundo Mariz; Stelios Tsigkos; Laura Fregonese; Stiina Aarum; Eleonora Dehlink; Jordi Llinares; Bruno Sepodes;
PUBLISHED: 2014, SOURCE: EXPERT OPINION ON ORPHAN DRUGS, VOLUME: 2, ISSUE: 11
INDEXED IN: Scopus WOS CrossRef
6
TITLE: Establishing medical plausibility in the context of orphan medicines designation in the European Union  Full Text
AUTHORS: Stelios Tsigkos; Segundo Mariz; Jordi Llinares; Laura Fregonese; Stiina Aarum; Naumann Winter Frauke; Kerstin Westermark; Bruno Sepodes;
PUBLISHED: 2014, SOURCE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 9, ISSUE: 1
INDEXED IN: Scopus WOS CrossRef
7
TITLE: European regulation on orphan medicinal products: 10 years of experience and future perspectives  Full Text
AUTHORS: Kerstin Westermark; Birthe Byskov Holm; Mirjam Soderholm; Jordi Llinares Garcia; Frida Riviere; Stiina Aarum; Florence Butlen Ducuing; Stelios Tsigkos; Agnieszka Wilk Kachlicka; Cinzia N'Diamoi;
PUBLISHED: 2011, SOURCE: NATURE REVIEWS DRUG DISCOVERY, VOLUME: 10, ISSUE: 5
INDEXED IN: WOS CrossRef: 81