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TITLE: Lysosomal and network alterations in human mucopolysaccharidosis type VII iPSC-derived neurons  Full Text
AUTHORS: Neus Bayo Puxan; Ana Paula Terrasso; Sophie Creyssels; Daniel Simao; Christina Begon Pescia; Marina Lavigne; Sara Salinas; Florence Bernex; Assumpcio Bosch; Vasiliki Kalatzis; Thierry Levade; Ana Maria Cuervo; Philippe Lory; Antonella Consiglio; Catarina Brito; Eric J Kremer;
PUBLISHED: 2018, SOURCE: SCIENTIFIC REPORTS, VOLUME: 8, ISSUE: 1
INDEXED IN: Scopus WOS
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TITLE: Disease-corrected haematopoietic progenitors from Fanconi anaemia induced pluripotent stem cells  Full Text
AUTHORS: Raya, A; Rodriguez Piz, I; Guenechea, G; Vassena, R; Navarro, S; Barrero, MJ; Consiglio, A; Castell, M; Rio, P; Sleep, E; Gonzalez, F; Tiscornia, G; Garreta, E; Aasen, T; Veiga, A; Verma, IM; Surralles, J; Bueren, J; Belmonte, JCI;
PUBLISHED: 2009, SOURCE: Nature, VOLUME: 460, ISSUE: 7251
INDEXED IN: Scopus CrossRef
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TITLE: Efficient and rapid generation of induced pluripotent stem cells from human keratinocytes  Full Text
AUTHORS: Aasen, T; Raya, A; Barrero, MJ; Garreta, E; Consiglio, A; Gonzalez, F; Vassena, R; Bilic, J; Pekarik, V; Tiscornia, G; Edel, M; Boue, S; Belmonte, JCI;
PUBLISHED: 2008, SOURCE: Nature Biotechnology, VOLUME: 26, ISSUE: 11
INDEXED IN: Scopus CrossRef