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TÍTULO: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis  Full Text
AUTORES: Alejandra Gonzalez Duarte; John L Berk; Dianna N Quan; Michelle L Mauermann; Hartmut H Schmidt; Michael Polydefkis; Marcia Waddington Cruz; Mitsuharu Ueda; Isabel M Conceicao; Arnt V Kristen; Teresa Coelho; Cecile A Cauquil; Celine Tard; Madeline Merkel; Emre Aldinc; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLICAÇÃO: 2020, FONTE: JOURNAL OF NEUROLOGY, VOLUME: 267, NÚMERO: 3
INDEXADO EM: Scopus WOS
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TÍTULO: Inotersen preserves or improves quality of life in hereditary transthyretin amyloidosis  Full Text
AUTORES: Teresa Coelho; Aaron Yarlas; Marcia Waddington Cruz; Michelle K White; Asia Sikora Kessler; Andrew Lovley; Michael Pollock; Spencer Guthrie; Elizabeth J Ackermann; Steven G Hughes; Chafic Karam; Sami Khella; Morie Gertz; Giampaolo Merlini; Laura Obici; Hartmut H Schmidt; Michael Polydefkis; James J B Dyck; Thomas H Brannagan; Isabel Conceicao; Merrill D Benson; John L Berk; ...Mais
PUBLICAÇÃO: 2020, FONTE: JOURNAL OF NEUROLOGY, VOLUME: 267, NÚMERO: 4
INDEXADO EM: Scopus WOS
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TÍTULO: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis (vol 264, pg 703, 2020)  Full Text
AUTORES: Alejandra Gonzalez Duarte; John L Berk; Dianna N Quan; Michelle L Mauermann; Hartmut H Schmidt; Michael Polydefkis; Marcia Waddington Cruz; Mitsuharu Ueda; Isabel M Conceicao; Arnt V Kristen; Teresa Coelho; Cecile A Cauquil; Celine Tard; Madeline Merkel; Emre Aldinc; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLICAÇÃO: 2020, FONTE: JOURNAL OF NEUROLOGY, VOLUME: 267, NÚMERO: 3
INDEXADO EM: WOS
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TÍTULO: Quality of life outcomes in APOLLO, the phase 3 trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis  Full Text
AUTORES: Laura Obici; John L Berk; Alejandra Gonzalez Duarte; Teresa Coelho; Julian Gillmore; Hartmut H J Schmidt; Matthias Schilling; Taro Yamashita; Celine Labeyrie; Thomas H Brannagan; Senda Ajroud Driss; Peter Gorevic; Arnt V Kristen; Jaclyn Franklin; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLICAÇÃO: 2020, FONTE: AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS, VOLUME: 27, NÚMERO: 3
INDEXADO EM: Scopus WOS
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TÍTULO: A phase II, open-label, extension study of long-term patisiran treatment in patients with hereditary transthyretin-mediated (hATTR) amyloidosis  Full Text
AUTORES: Teresa Coelho; David Adams; Isabel Conceicao; Marcia Waddington Cruz; Hartmut H Schmidt; Juan Buades; Josep Campistol; John L Berk; Michael Polydefkis; Jing Jing Wang; Jihong H Chen; Marianne T Sweetser; Jared Gollob; Ole B Suhr;
PUBLICAÇÃO: 2020, FONTE: ORPHANET JOURNAL OF RARE DISEASES, VOLUME: 15, NÚMERO: 1
INDEXADO EM: Scopus WOS
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TÍTULO: "Red-flag" symptom clusters in transthyretin familial amyloid polyneuropathy  Full Text
AUTORES: Isabel Conceicao; Alejandra Gonzalez Duarte; Laura Obici; Hartmut H J Schmidt; Damien Simoneau; Moh Lim Ong; Leslie Amass;
PUBLICAÇÃO: 2016, FONTE: JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM, VOLUME: 21, NÚMERO: 1
INDEXADO EM: WOS
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TÍTULO: Management of asymptomatic gene carriers of transthyretin familial amyloid polyneuropathy. TTR-FAP Gene Carriers  Full Text
AUTORES: Hartmut H J Schmidt; Fabio Barroso; Alejandra Gonzalez Duarte; Isabel Conceicao; Laura Obici; Denis Keohane; Leslie Amass;
PUBLICAÇÃO: 2016, FONTE: MUSCLE & NERVE, VOLUME: 54, NÚMERO: 3
INDEXADO EM: Scopus WOS CrossRef
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TÍTULO: PATISIRAN PH 2 OPEN-LABEL EXTENSION STUDY IN FAMILIAL AMYLOIDOTIC POLYNEUROPATHY
AUTORES: Hartmut Schmidt; David Adams; Teresa Coelho; Isabel Conceicao; Marcia Waddington Cruz; Juan Buades; Josep Campistol; Jean Pouget; Jared Gollob; Ole Suhr;
PUBLICAÇÃO: 2016, FONTE: Annual Meeting of the Association-of-British-Neurologists (ABN) in JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, VOLUME: 87, NÚMERO: 12
INDEXADO EM: WOS
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TÍTULO: Diagnosis, Prognosis, and Therapy of Transthyretin Amyloidosis  Full Text
AUTORES: Morie A Gertz; Merrill D Benson; Peter J Dyck; Martha Grogan; Terresa Coelho; Marcia Cruz; John L Berk; Violaine Plante Bordeneuve; Hartmut H J Schmidt; Giampaolo Merlini;
PUBLICAÇÃO: 2015, FONTE: JOURNAL OF THE AMERICAN COLLEGE OF CARDIOLOGY, VOLUME: 66, NÚMERO: 21
INDEXADO EM: WOS CrossRef
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TÍTULO: PHASE 2 OPEN-LABEL EXTENSION STUDY OF PATISIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC FOR THE TREATMENT OF FAMILIAL AMYLOID POLYNEUROPATHY
AUTORES: David Adams; Ole Suhr; Isabel Conceicao; Marcia Waddington Cruz; Hartmut Schmidt; Juan Buades; Josep Campistol; Jean Pouget; John Berk; Teresa Coelho;
PUBLICAÇÃO: 2015, FONTE: Annual Meeting of the Association-of-British-Neurologists (ABN) in JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, VOLUME: 86, NÚMERO: 11
INDEXADO EM: WOS CrossRef
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