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TITLE: Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease
AUTHORS: Biegstraaten, M; Cox, TM; Belmatoug, N; Berger, MG; Collin Histed, T; Vom Dahl, SV; Di Rocco, M; Fraga, C; Giona, F; Giraldo, P; Hasanhodzic, M; Hughes, DA; Iversen, PO; Kiewiet, AI; Lukina, E; Machaczka, M; Marinakis, T; Mengel, E; Pastores, GM; Ploeckinger, U; Rosenbaum, H; Serratrice, C; Symeonidis, A; Szer, J; Timmerman, J; Tylki Szymanska, A; Weisz W Hubshman; Zafeiriou, DI; a Zimran; Hollak, CEM; ...More
PUBLISHED: 2018, SOURCE: BLOOD CELLS MOLECULES AND DISEASES, VOLUME: 68
INDEXED IN: WOS