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TITLE: Stakeholder cooperation to overcome challenges in orphan medicine development: the example of Duchenne muscular dystrophy  Full Text
AUTHORS: Volker Straub; Pavel Balabanov; Kate Bushby; Monica Ensini; Nathalie Goemans; Annamaria De Luca; Alejandra Pereda; Robert Hemmings; Giles Campion; Edward Kaye; Virginia Arechavala Gomeza; Aurelie Goyenvalle; Erik Niks; Olav Veldhuizen; Pat Furlong; Violeta Stoyanova Beninska; Matthew J Wood; Alex Johnson; Eugenio Mercuri; Francesco Muntoni; Bruno Sepodes; Manuel Haas; Elizabeth Vroom; Annemieke Aartsma Rus; ...More
PUBLISHED: 2016, SOURCE: LANCET NEUROLOGY, VOLUME: 15, ISSUE: 8
INDEXED IN: Scopus WOS CrossRef