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TÍTULO: Treatment response and neurofilament light chain levels with long-term patisiran in hereditary transthyretin-mediated amyloidosis with polyneuropathy: 24-month results of an open-label extension study  Full Text
AUTORES: Simina Ticau; Emre Aldinc; Michael Polydefkis; David Adams; Teresa Coelho; Mitsuharu Ueda; Cecilia Hale; John Vest; Paul Nioi;
PUBLICAÇÃO: 2023, FONTE: AMYLOID-JOURNAL OF PROTEIN FOLDING DISORDERS
INDEXADO EM: Scopus WOS
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TÍTULO: Analysis of autonomic outcomes in APOLLO, a phase III trial of the RNAi therapeutic patisiran in patients with hereditary transthyretin-mediated amyloidosis  Full Text
AUTORES: Alejandra Gonzalez Duarte; John L Berk; Dianna N Quan; Michelle L Mauermann; Hartmut H Schmidt; Michael Polydefkis; Marcia Waddington Cruz; Mitsuharu Ueda; Isabel M Conceicao; Arnt V Kristen; Teresa Coelho; Cecile A Cauquil; Celine Tard; Madeline Merkel; Emre Aldinc; Jihong H Chen; Marianne T Sweetser; Jing Jing Wang; David Adams;
PUBLICAÇÃO: 2020, FONTE: JOURNAL OF NEUROLOGY, VOLUME: 267, NÚMERO: 3
INDEXADO EM: Scopus WOS