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TITLE: Clinical effect and safety profile of pegzilarginase in patients with arginase 1 deficiency  Full Text
AUTHORS: Diaz, GA; Schulze, A; McNutt, MC; Leao Teles, E; Merritt, JL; Enns, GM; Batzios, S; Bannick, A; Zori, RT; Sloan, LS; Potts, SL; Bubb, G; Quinn, AG;
PUBLISHED: 2021, SOURCE: JOURNAL OF INHERITED METABOLIC DISEASE
INDEXED IN: Scopus WOS