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TITLE: Counteracting chromatin effects of a splicing-correcting antisense oligonucleotide improves its therapeutic efficacy in spinal muscular atrophy
AUTHORS: Marasco, Luciano E.; Dujardin, Gwendal; Sousa Luis, Rui; Liu, Ying Hsiu; Stigliano, Jose N.; Nomakuchi, Tomoki; Proudfoot, Nick J.; Krainer, Adrian R.; Kornblihtt, Alberto R.;
PUBLISHED: 2022, SOURCE: CELL, VOLUME: 185, ISSUE: 12
INDEXED IN: Scopus WOS