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TITLE: Lentiviral gene therapy reverts GPIX expression and phenotype in Bernard-Soulier syndrome type C
AUTHORS: Martinez Navajas, Gonzalo; Ceron Hernandez, Jorge; Simon, Iris; Lupianez, Pablo; Diaz McLynn, Sofia; Perales, Sonia; Modlich, Ute; Guerrero, Jose A.; Martin, Francisco; Sevivas, Teresa; Lozano, Maria L.; Rivera, Jose; Ramos Mejia, Veronica; Tersteeg, Claudia; Real, Pedro J.;
PUBLISHED: 2023, SOURCE: MOLECULAR THERAPY-NUCLEIC ACIDS, VOLUME: 33
INDEXED IN: Scopus WOS