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TITLE: Safety, pharmacokinetics, and pharmacodynamics of oral venglustat in Parkinson disease patients with a GBA mutation from Japan and the rest of the world: Results from part 'I of the MOVES-PD study  Full Text
AUTHORS: Judith J Peterschmitt; Hidemoto Saiki; Taku Hatano; Thomas Gasser; Stuart Isaacson; Jaime Kulisevsky; Tanya Simuni; Yuji Takahashi; Anne Marie Wills; Leonor Correia Guedes; Per Svenningsson; Ryosuke Takahashi; Cheryl Waters; Masahisa Katsuno; Allena Ji Ji; Sebastiaan J M Gaemers; Pascal Minini; Blandine Nembo; Pablo Sardi; Stephane Saubadu; Jyoti Sharma; Tanya Fischer; ...More
PUBLISHED: 2020, SOURCE: 16th Annual Research Meeting of the WORLDSymposium(TM) in MOLECULAR GENETICS AND METABOLISM, VOLUME: 129, ISSUE: 2
INDEXED IN: WOS
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TITLE: Safety, Pharmacokinetics, and Pharmacodynamics of Oral Venglustat in the Japanese and the Rest of the World Parkinson's Disease Population With a GBA Mutation: Results from Part 1 of the MOVES-PD Study
AUTHORS: Judith J Peterschmitt; Hidemoto Saiki; Taku Hatano; Thomas Gasser; Stuart Isaacson; Jaime Kulisevsky; Tanya Simuni; Yuji Takahashi; Anne Marie Wills; Leonor Correia Guedes; Per Svenningsson; Ryosuke Takahashi; Cheryl Waters; Masahisa Katsuno; Allena Ji Ji; Sebastiaan J M Gaemers; Pascal Minini; Blandine Nembo; Pablo Sardi; Stephane Saubadu; Jyoti Sharma; Tanya Fischer; ...More
PUBLISHED: 2020, SOURCE: Annual Meeting of the American-Academy-of-Neurology in NEUROLOGY, VOLUME: 94, ISSUE: 15
INDEXED IN: WOS
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TITLE: Safety, tolerability and pharmacokinetics of oral venglustat in Parkinson disease patients with a GBA mutation  Full Text
AUTHORS: Judith J Peterschmitt; Thomas Gasser; Stuart Isaacson; Jaime Kulisevsky; Pablo Mir; Tanya Simuni; Anne Marie Wills; Leonor Correia Guedes; Per Svenningsson; Cheryl Waters; Allena J Ji; Jian Li; Pascal Minini; Blandine Nembo; Stephane Saubadu; Jyoti Sharma; Tanya Fischer;
PUBLISHED: 2019, SOURCE: 15th Annual Research Meeting of the WORLDSymposium(TM) in MOLECULAR GENETICS AND METABOLISM, VOLUME: 126, ISSUE: 2
INDEXED IN: WOS
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TITLE: Addendum to Letter to the Editor: Safety, efficacy, and authorization of eliglustat as a first-line therapy in Gaucher disease type 1  Full Text
AUTHORS: Pramod K Mistry; Manisha Balwani; Hagit N Baris; Hadhami Ben Turkia; Andrew A Burrow; Joel Charrow; Gerald F Cox; Sumita Danda; Marta Dragosky; Guillermo Drelichman; Amal El Beshlawy; Cristina Fraga; Selena Freisens; Sebastiaan Gaemers; Evgueniy Hadjiev; Priya S Kishnani; Elena Lukina; Pierre Maison Blanche; Ana Maria Martins; Gregory Pastores; Milan Petakov; Judith J Peterschmitt; Hanna Rosenbaum; Barry Rosenbloom; Lisa H Underhill; Timothy M Cox; ...More
PUBLISHED: 2019, SOURCE: BLOOD CELLS MOLECULES AND DISEASES, VOLUME: 77
INDEXED IN: Scopus WOS
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TITLE: Once- versus twice-daily dosing of eliglustat in adults with Gaucher disease type 1: The Phase 3, randomized, double-blind EDGE trial  Full Text
AUTHORS: Joel Charrow; Cristina Fraga; Xuefan F Gu; Hiroyuki Ida; Nicola Longo; Elena Lukina; Alexandre Nonino; Sebastiaan J M Gaemers; Marie Helene Jouvin; Jing Li; Yaoshi S Wu; Yong Xue; Judith J Peterschmitt;
PUBLISHED: 2018, SOURCE: MOLECULAR GENETICS AND METABOLISM, VOLUME: 123, ISSUE: 3
INDEXED IN: WOS